A poorly characterized protein, historically thought to be a chaperon or enzyme, may actually be a key player in prostate ...

St. Jude researchers advance CASTs, enhancing precision and activity for next-generation genome-editing therapies.

NEW YORK, NY – Two prominent biotechnology companies, Vertex Pharmaceuticals and CRISPR Therapeutics, both led by Indian American CEOs, have been named to TIME’s 2025 list of the 100 Most Influential ...

In the five years since Italy-based Chiesi Group established its rare disease division in Boston, the unit has landed regulatory approvals worldwide for 10 therapies — all small molecules and ...

CRISPR Therapeutics (CRSP) reported new preclinical data from its novel SyNTase gene editing platform for the treatment of Alpha-1 Antitrypsin Deficiency, AATD. The data are featured in an oral ...

Iranian filmmaker Jafar Panahi’s latest feature, It Was Just an Accident, is among the leading nominees for this year’s Asia Pacific Screen Awards (APSA) with two nods, including the gong for Best ...

Jeanette Henriquez, on the left, stands with her two children, Jasmine Henriquez and Dominic Henriquez. Dominic Henriquez was diagnosed with Hunter Syndrome in 2011 before the condition was added to ...

Newborn babies in England will be routinely screened for a rare genetic condition that can cause long-term health problems if left untreated, officials have announced. Hereditary tyrosinaemia type 1 ...