The FDA previously placed two clinical studies on hold, including the Phase III trial in which the liver toxicity occurred.

Explore CRISPR technology explained, gene editing science, DNA modification, and genetic engineering ethics—discover how ...

Recognized in the Biotechnology category of the 2025 Top Innovations contest, small Cas12l nucleases are versatile, ...

Jarome and his team found that aging disrupts K63 polyubiquitination in two distinct areas of the brain. In the hippocampus, ...

Technology opens the door to more accurate preclinical testing, which could enable the development of safer and more effective therapies.

It is a smart strategy to diversify your portfolio by investing in high-quality companies built on proven technologies.

Stanford researchers and their collaborators have revealed a new device that could change the way scientists conduct gene-editing experiments. The device, CRISPR-GPT, is an artificial intelligence lab ...

Cutting-edge gene editing technology could eradicate Down syndrome, according to Japanese scientists. Down syndrome, which causes a range of developmental differences and affects 1 in 700 newborns in ...

Both CRSP and NTLA are advancing in vivo gene editing therapies targeting large markets, with financial stability supporting ongoing R&D and commercialization plans. Investors should note the binary ...

The baby's disease prevented the liver from removing ammonia Half of babies with the disease die in their first week of life The baby has already shown signs of improvement The baby's disease ...

Developing a gene therapy typically takes years, but when Baby KJ was diagnosed with a deadly genetic condition, scientists had only months. What followed was a successful collaboration among ...

Emerging genetics research could help brands create mainstream wheat products that are safer for gluten-sensitive consumers – ...