Some of the most expensive drugs currently in use are gene therapies to treat specific diseases, and their high cost limits ...

Jason Mast is a general assignment reporter at STAT focused on the science behind new medicines and the systems and people that decide whether that science ever reaches patients. You can reach Jason ...

An experimental gene therapy developed by researchers at UCLA, University College London and Great Ormond Street Hospital has restored and maintained immune system function in 59 of 62 children born ...

The FDA is investigating the deaths of two boys with Duchenne muscular dystrophy who died soon after being treated with delandistrogene moxeparvovec (Elevidys) gene therapy, the agency said. The ...

These long-term findings in a large patient cohort show the sustained clinical efficacy and safety of autologous CD34+ hematopoietic stem-cell lentiviral gene therapy for ADA-SCID, indicating that it ...

England's AviadoBio is looking to China as a potential source of additional gene therapies, securing an option to a $413 million biobucks deal that could deliver a clinical-stage rare eye disease ...

Shocking health announcement coming from the Biden family. Former President Joe Biden diagnosed with an aggressive form of prostate cancer that has spread to his bones. His personal office releasing ...

A 3-year-old girl who underwent a breakthrough gene therapy treatment to treat profound hearing loss can hear on her own, two years after the treatment. Opal Sandy made history in 2023 when at 11 ...

Scientists have reversed diabetic heart failure with a genetic therapy in mice and miniature human "hearts" grown from stem cells. The new gene therapy may be a promising treatment for diabetic heart ...

Joe Biden has started radiation therapy as part of his treatment for prostate cancer, a spokesperson for the former president told CNN. “As part of a treatment plan for prostate cancer, President ...

Opal Sandy, now 3, underwent a gene therapy injection to her right ear in 2023. Trump administration looking to sell nearly 200 commissary stores Smith Says Trump Knowingly Withheld Classified ...

Former President Joe Biden has started radiation therapy as part of his treatment for prostate cancer, a spokesperson for the former president told CNN.Video above from May 2025: Former President Joe ...