Regenxbio's RGX-121 gene therapy for Hunter syndrome is the main catalyst, with FDA approval targeted for February 2026.

FDA launches Rare Disease Evidence Principles to guide therapy reviews, offering new pathways for approval while raising ...

A Louisville man who survived being shot in the head along Interstate 65 is now making progress at a rehabilitation center ...

Joe Burrow's journey to recovery from a Grade III turf toe injury is expected to be challenging, according to several ...

An immigrant rights advocate said attorneys and immigration advocates were trying to figure out if transgender immigrants’ ...

On Tuesday, OpenAI announced plans to develop an automated age-prediction system that will determine whether ChatGPT users ...

Arnold Schwarzenegger and Heather Milligan's relationship spans over a decade, from red carpet appearances to meaningful ...

Think you know everything about minimally invasive spine surgery in Clifton? Discover crucial insights that could change your ...

It is understood that Kunya did not give up after his injury; instead, he has been working twice as hard on his rehabilitation training. Manchester United's head coach, Amorim, has also expressed ...

Special CallCompany ParticipantsGuido Oelkers - CEO & PresidentMatthew WinfieldConference Call ParticipantsHerbert S.